Global Launch Strategy for a Rare Diseases Company

Aim

Our aim was to support a small, specialist rare diseases company with the global launch of their novel product for an ultra-rare condition, by acting as a true strategic partner delivering seamless and adaptable support across medical communications, evidence generation and market access, alongside agile insourcing, ensuring a cohesive launch strategy.

Approach

We worked as strategic partners with our client, providing tailored support across multiple workstreams with a global scope. Our Value and Access, Medical Affairs, Evidence Generation and Publications workstreams each had a dedicated, senior workstream lead, ensuring leadership and expertise in each area. Our workstream leads collaborated closely alongside an overall account manager to deliver a flexible and aligned service ensuring seamless integration across the various project types:

• Partnership with senior client stakeholders to develop and implement a comprehensive market access strategy alongside development of global market access materials
• Development of compelling and cohesive messaging across medical communications, which complemented the market access strategy
• Publications planning and development, to disseminate key messages and evidence at the right time
• Medical education support and on-site event support, working flexibly to adapt the strategy based on insights gathered in the field
• Design and conduct of tailored evidence generation activities, applying strategic and data-driven methodologies suitable for an ultra-orphan condition to meet specific market access requirements

Impact

• A true, strategic partnership that fostered close collaboration with the client
• A team structure that allowed the provision of comprehensive, expert support, with an ability to adapt our resourcing to respond to changes in client priorities
• Persuasive and cohesive messaging aligned across all medical communications, health technology assessment submissions and global value materials
• Comprehensive and compelling global value materials, used widely across cross-functional teams
• Successfully held a range of medical events to gather expert opinion and build the client’s reputation in the clinical community
• Early identification of key evidence gaps and risks for health technology assessment, with effective mitigation recommendations and comprehensive support for generating high-quality evidence