We tailor our services to:

Assess and address the lack of good quality clinical and health economic evidence using state of the art evidence generation methodologies

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Provide a clear, engaging and strategic approach to communications with a wide range of stakeholders to address the poor awareness and understanding of rare conditions in the wider community

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Effectively communicate the value of orphan and ultra orphan products to address the higher degree of uncertainty inherent to their evidence bases

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Evidence Development

  • Systematic and targeted literature reviews
  • Delphi panels
  • Cost and resource use studies
  • Survey design and analysis
  • Gap analysis and evidence generation recommendations
  • Utility studies
  • Structured expert elicitation, including Delphi panels

Value & Access

  • Global HTA
  • Health economic modelling, including early pricing models
  • Value proposition creation and value dossier development
  • AMCP dossiers
  • Pre-approval information exchange decks

Medical Communications

  • Advisory boards
  • Scientific communication platforms
  • Strategic publication planning, manuscripts and conference support
  • Multistakeholder workshops
  • Patient materials
  • Key opinion leader mapping
  • Enhanced publications content, including lay summaries

What sets our Rare Diseases service offerings apart?

  • Exceptional customer service
  • Provision of a single, consistent project team with rare disease-specific experience tailored to the needs of your project
  • Commitment to patient-centricity, ensuring the voice of patients with rare diseases is at the heart of what we do
  • Clear and transparent project budgets
  • Commitment to the active contribution of novel rare diseases research
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Maximising the value of expert judgement in rare diseases

The Rare Diseases team at Costello Medical is undertaking a research project in collaboration with Sheela Upadhyaya, exploring how expert judgement could be best used to support the development of and patient access to rare disease therapies. If you would like to be kept up to date with the progress of this research project, please register your interest below.

We recently developed a short guide, which introduces expert judgement, and provides an overview of its current use in rare diseases. This guide can be accessed here.

Register For Updates

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Overcoming challenges in rare diseases

Our Rare Diseases team are committed to actively contributing research to overcome the challenges faced by industry and the patient community. Our research contributions include peer-reviewed manuscripts, panels and posters, to high impact journals and international conferences such as ISPOR and ISMPP.

Learn More

For more information on our Rare Diseases services or to request a quote, please contact Annabel Griffiths

Get In Touch

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