In celebration of Rare Disease Day, we were delighted to participate in the 2021 Rare Diseases campaign led by a number of fantastic organisations such as Genetic Alliance UK, ERN-RND and Same but Different. The full publication is available at and was published in the Guardian. Our Head of Rare Diseases, Annabel Griffiths, shares her thoughts on addressing uncertainty in rare disease therapies here – let us know what you think!

If you’d like to find out more about our expertise and services in rare diseases, visit our Rare Diseases page or contact Annabel Griffiths.

View the full publication